“Saving Lives with Gene Replacement Therapy”: ABC News
Check out this news story about how gene replacement therapy has been a game changer for neuromuscular disorders, especially babies diagnosed with Spinal Muscular Atrophy.
Utah Toddler One Of First To Receive Groundbreaking Gene Replacement Therapy, 26 August 2020
See below for the miraculous story of one of Dr. Butterfield’s Spinal Muscular Atrophy patients who received groundbreaking gene therapy replacement therapy through one of our clinical trials!
Researchers Hope Experimental Gene Therapy Is An Answer To A Fatal Genetic Disorder
Check out this moving NPR story, by Jon Hamilton, with a spotlight on the first patient on the Pfizer Gene Therapy Clinical Trial for Duchenne Muscular Dystrophy. UPIN is currently a selected site for this clinical trial! For more information on current enrollment, check out our Clinical Trials page to contact the appropriate Clinical Research…